Gene Therapy for Beta-Thalassemia (HGI-001 Injection)
Treatment of transfusion-dependent β-thalassemia using modified autologous hematopoietic stem cells.
Pipelines
InVitro Therapy
Gene Therapy for Alpha-Thalassemia (HGI-002 Injection)
Treatment of transfusion-dependent α-thalassemia using modified autologous hematopoietic stem cells.
Gene Therapy for Wiskott-Aldrich Syndrome (WAS)
Explore options for the treatment of WAS syndrome using lentiviral vectors.
Gene Therapy for Severe Combined Immunodeficiency Disease (SCID)
Severe Combined Immunodeficiency Disease (SCID) is a rare childhood disease and is one of the most serious types of primary immunodeficiency diseases.
Gene Therapy for Metachromatic leukodystrophy (MLD)
Discover innovative gene therapies for treating and/or alleviating neurodegenerative diseases.